In this webinar – ‘Enabling Digitally Enhanced Care for Rare Diseases in Europe: Integrating AI and Connected Care ...

With the annual cost estimated to be about ₹1 crore for each child requiring treatment for ultra-rare diseases, the Medical ...

Bengaluru: The medical education department is reaching out to corporate entities for support in treating children affected ...

GT-02287 oral presentation demonstrates new evidence of disease-modifying capacity in GBA1 and idiopathic Parkinson's disease ...

BENGALURU: Medical Education and Skill Development Minister Dr Sharan Prakash Patil has urged corporate houses, to adopt kids ...

Rocket Pharmaceuticals' gene therapies offer long-term effects for cardiovascular and hematology diseases. Read why I rate ...

The Greenwood Genetic Center has designed a functional platform to assess the pathogenicity of variants of uncertain significance in IDUA identified by newborn screening for MPS I. With further ...

In the self-filmed spinoff series, Anny took viewers into her home, where she showed off her late son, Adriel’s belongings. Anny, who was pregnant with her third child, son Eliel, at the time of ...

Chiesi GRD has an initial focus in developing therapies for lysosomal storage disorders (LSDs), including Fabry disease, as well as other rare diseases in haematology and opthalmology indications.

Sangamo Therapeutics, Inc.'s $18M Eli Lilly deal boosts CNS genomic medicines. Fabry gene therapy data in 2025 is key for ...

Raymond James Financial Inc. purchased a new stake in Denali Therapeutics Inc. (NASDAQ:DNLI – Free Report) during the fourth ...